Search Results for: CRISPR for sickle cell disease

Weekly reads: stem cell good news, bad news on sickle cell, MS, IPSCs

/ / 1 Comment
victoria gray family crispr sickle cell b

Let’s start with some stem cell good news on evolving approaches to treat sickle cell disease involving stem cells. Then on another related front things were more concerning. Stem cell good news on sickle cell disease, a complication Sickle Cell Disease News reports Adding Briquilimab Boosts Success of Sickle Cell Stem Cell Transplant. This is a […]

Weekly reads: stem cell good news, bad news on sickle cell, MS, IPSCs Read More »

He Jiankui says he’s back in the lab after prison for CRISPR babies

/ / Leave a Comment
He Jiankui

Earlier this year Chinese researcher He Jiankui finished his prison sentence. When I saw that news I wondered about the next chapter for him. It seems he’s already back in the lab doing genetics research. At least that’s according to a blog by He Jiankui himself. Can we trust that what he has written on his website is

He Jiankui says he’s back in the lab after prison for CRISPR babies Read More »

Updates on CRISPR therapy development and clinical trials

/ / Leave a Comment

When I first heard of CRISPR gene editing I was excited for my lab to try it out, but it seemed a long way from the field having even one CRISPR therapy available to treat human disease. In the Knoepfler lab, we study genetic and genomic programming in human development and disease. Gene editing seemed

Updates on CRISPR therapy development and clinical trials Read More »

Weekly reads: death in CRISPR trial, sickle cell, nose picking & dementia, epilepsy

/ / Leave a Comment
CRISPR gene editing

As both a scientist who works on stem cells, cancer, and CRISPR, and a research advocate I’ve been fortunate to meet many patient advocates over the years. Some have been participants in clinical trials themselves. Benefits & risks of clinical trial participation It is very sobering to find out that a clinical trial participant has

Weekly reads: death in CRISPR trial, sickle cell, nose picking & dementia, epilepsy Read More »

Weekly stem cell reads: space, plagiarism, HIV, diabetes, more

/ / Leave a Comment
blood stem cell biology

I took a cross-country road trip earlier this month that was pretty amazing and barely thought about stem cell research for the first time in years. We did run across one stem cell clinic in Florida by accident. I’ll write about that trip soon, but first we have our weekly reads including some very cool

Weekly stem cell reads: space, plagiarism, HIV, diabetes, more Read More »

Grading my 21 stem cell & regenerative medicine predictions for 2021

/ / 3 Comments
stem-cell-crystal-ball-300x3001

The world of stem cell research and regenerative medicine is unpredictable but it’s fun to be a part of it and try to do predictions. Each year in late December or early January I make prognostications for the coming year for stem cell research and regenerative medicine. I made 21 such predictions for the current

Grading my 21 stem cell & regenerative medicine predictions for 2021 Read More »

Recommended reads: CRISPR for Sickle Cell, Parkinson’s, & more

/ / Leave a Comment
victoria gray family crispr sickle cell b

I’m playing catch-up on some reading given how busy I’ve been and this includes a groundbreaking NEJM pub on CRISPR for Sickle Cell and Thalassemia. CRISPR for Sickle Cell From December, here’s the key paper in the NEJM: CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia. There’s a lot to like about this clinical

Recommended reads: CRISPR for Sickle Cell, Parkinson’s, & more Read More »